
Ultragenyx Pharmaceutical (RARE) Stock Forecast & Price Target
Ultragenyx Pharmaceutical (RARE) Analyst Ratings
Bulls say
Ultragenyx Pharmaceutical Inc. has demonstrated a strong positive outlook due to the compelling 96-week data from its Phase 3 study of DTX401, confirming its potential as a first-in-class treatment for glycogen storage disease type 1a (GSD1a). The data highlight a durable and transformative benefit, including effective glycemic control with low rates of hypoglycemia and improved fasting tolerance, which enhances the therapy's appeal in the market. These findings suggest a significant risk mitigation for the DTX401 program, reinforcing expectations for its 2026 launch and its potential for meaningful commercial success in addressing a critical unmet need in the treatment of rare diseases.
Bears say
The financial outlook for Ultragenyx Pharmaceutical Inc. is hindered by several significant risks that could adversely affect its performance. Key concerns include the potential for clinical trial failures, delays or failures in securing regulatory approvals for critical products such as UX111 and setrusumab, and the risk of lower-than-expected sales due to competitive market dynamics and pricing pressures. Additionally, the company faces uncertainty from patent challenges and increased regulatory scrutiny specifically related to gene therapies, which could further impede its growth and profitability.
This aggregate rating is based on analysts' research of Ultragenyx Pharmaceutical and is not a guaranteed prediction by Public.com or investment advice.
Ultragenyx Pharmaceutical (RARE) Analyst Forecast & Price Prediction
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